U01.15.003 Teratogens

Learning Objectives

Master the Comprehensive List of Teratogens and their specific clinical impacts. Understand the windows of susceptibility and recognize the distinct “signature” defects associated with specific medications and maternal conditions for the USMLE Step 1.


1. Principles of Teratogenicity

Susceptibility to teratogens varies with the developmental stage at the time of exposure.

Period Timing Effect
Pre-implantation Weeks 1–2 “All-or-none” effect.
Embryonic Period Weeks 3–8 Organogenesis: Highest susceptibility to structural defects.
Fetal Period Week 8+ Affects growth and function.

2. Teratogenic Medications

The following medications are known to cause specific, predictable malformations.

Medication Clinical Effect on Fetus
ACE Inhibitors Renal failure, Oligohydramnios, and hypocalvaria.
Alkylating agents Multiple anomalies (e.g., ear/facial abnormalities, absence of digits).
Aminoglycosides Ototoxicity (“A mean guy hit the baby in the ear”).
Antiepileptics Neural tube defects, cardiac defects, cleft palate, and phalanx/nail hypoplasia. (High-dose folate recommended).
Diethylstilbestrol Vaginal clear cell adenocarcinoma, congenital Müllerian anomalies.
Fluoroquinolones Cartilage damage.
Folate antagonists Neural tube defects (Trimethoprim, Methotrexate).
Isotretinoin Craniofacial, CNS, cardiac, and Thymic defects. (Contraception is mandatory).
Lithium Ebstein anomaly (apical displacement of the tricuspid valve).
Methimazole Aplasia cutis congenita (congenital absence of scalp skin).
Tetracyclines Discolored teeth (“Teethracyclines”) and inhibited bone growth.
Thalidomide Limb defects (Phocomelia/flipper limbs).
Warfarin Stippled epiphyses (bone/cartilage deformities) and nasal hypoplasia. Use Heparin instead.

 


3. Substance Use & Other Factors

Environmental exposures and maternal health states significantly influence fetal outcomes.

Exposure Effect on Fetus
Alcohol Fetal Alcohol Syndrome (intellectual disability, facial dysmorphism).
Cocaine Preterm birth and Fetal Growth Restriction (FGR) via vasoconstriction.
Tobacco Low birth weight (leading cause in resource-rich areas), SIDS, and ADHD.

4. Other Factors

Environmental exposures and maternal health states significantly influence fetal outcomes.

Exposure Effect on Fetus
Iodine (Lack/Excess) Congenital hypothyroidism.
Maternal Diabetes Caudal regression syndrome, transposition of great arteries (TGA), and Macrosomia.
Maternal PKU Microcephaly, intellectual disability, and heart defects.
Methylmercury Neurotoxicity (found in large predator fish).
X-rays Microcephaly and intellectual disability. Lead shielding minimizes risk.

Activity


High-Yield Mnemonics & Tips:

  • Aminoglycosides: “A mean guy hit the baby in the ear” (Ototoxicity).
  • Warfarin: “In war, you need strong bones to march and optics to see the enemy” (Bone deformities, Optic nerve atrophy).
  • Maternal Diabetes: Classic for Caudal Regression Syndrome (agenesis of the sacrum/lumbar spine).
  • Isotretinoin: Contraception is vital because of Thymic and cardiac malformations.

Activity: